Succinic semialdehyde dehydrogenase deficiency, a disorder of GABA metabolism: an update on pharmacological and enzyme-replacement therapeutic strategies

Kara R. Vogel, Garrett R. Ainslie, Dana C. Walters, Alice McConnell, Sameer C. Dhamne, Alexander Rotenberg, Jean Baptiste Roullet, K. Michael Gibson

Research output: Contribution to journalArticlepeer-review

29 Scopus citations

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