Optimized adeno-associated virus (AAV)-protein phosphatase-5 helper viruses for efficient liver transduction by single-stranded AAV vectors: Therapeutic expression of factor IX at reduced vector doses

Giridhara R. Jayandharan, Li Zhong, Brandon K. Sack, Angela E. Rivers, Mengxin Li, Baozheng Li, Roland W. Herzog, Arun Srivastava

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Medicine & Life Sciences