Optimized adeno-associated virus (AAV)-protein phosphatase-5 helper viruses for efficient liver transduction by single-stranded AAV vectors: Therapeutic expression of factor IX at reduced vector doses
Giridhara R. Jayandharan, Li Zhong, Brandon K. Sack, Angela E. Rivers, Mengxin Li, Baozheng Li, Roland W. Herzog, Arun Srivastava
Research output: Contribution to journal › Article › peer-review
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