Duvoglustat HCl Increases Systemic and Tissue Exposure of Active Acid α-Glucosidase in Pompe Patients Co-administered with Alglucosidase α

Priya Kishnani, Mark Tarnopolsky, Mark Roberts, Kumarswamy Sivakumar, Majed Dasouki, Mazen M. Dimachkie, Erika Finanger, Ozlem Goker-Alpan, Karl A. Guter, Tahseen Mozaffar, Muhammad Ali Pervaiz, Pascal Laforet, Todd Levine, Matthews Adera, Richard Lazauskas, Sheela Sitaraman, Richie Khanna, Elfrida Benjamin, Jessie Feng, John J. FlanaganJay Barth, Carrolee Barlow, David J. Lockhart, Kenneth J. Valenzano, Pol Boudes, Franklin K. Johnson, Barry Byrne

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