Curative ex vivo liver-directed gene therapy in a pig model of hereditary tyrosinemia type 1

Raymond D. Hickey, Shennen A. Mao, Jaime Glorioso, Faysal Elgilani, Bruce Amiot, Harvey Chen, Piero Rinaldo, Ronald Marler, Huailei Jiang, Timothy R. DeGrado, Lukkana Suksanpaisan, Michael K. O'Connor, Brittany L. Freeman, Samar H. Ibrahim, Kah Whye Peng, Cary O. Harding, Chak Sum Ho, Markus Grompe, Yasuhiro Ikeda, Joseph B. LillegardStephen J. Russell, Scott L. Nyberg

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