Unwarranted, long term, alglucosidase alfa enzyme replacement therapy in two non-Pompe disease patients

Chafic Karam, Thomas Ragole, Orly Moshe-Lilie, Nizar Chahin

Research output: Contribution to journalArticlepeer-review

Original languageEnglish (US)
Article number106048
JournalClinical Neurology and Neurosurgery
Volume196
DOIs
StatePublished - Sep 2020

Keywords

  • LOPD
  • Misdiagnosis
  • Pompe disease

ASJC Scopus subject areas

  • Surgery
  • Clinical Neurology

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