Self-reported treatment-associated symptoms among patients with urea cycle disorders participating in glycerol phenylbutyrate clinical trials

Sandesh C.S. Nagamani, George A. Diaz, William Rhead, Susan A. Berry, Cynthia Le Mons, Uta Lichter-Konecki, James Bartley, Annette Feigenbaum, Andreas Schulze, Nicola Longo, William Berquist, Renata Gallagher, Dennis Bartholomew, Cary O. Harding, Mark S. Korson, Shawn E. McCandless, Wendy Smith, Jerry Vockley, David Kronn, Robert ZoriStephen Cederbaum, J. Lawrence Merritt, Derek Wong, Dion F. Coakley, Bruce F. Scharschmidt, Klara Dickinson, Miguel Marino, Brendan H. Lee, Masoud Mokhtarani

Research output: Contribution to journalArticlepeer-review

15 Scopus citations

Fingerprint

Dive into the research topics of 'Self-reported treatment-associated symptoms among patients with urea cycle disorders participating in glycerol phenylbutyrate clinical trials'. Together they form a unique fingerprint.

Medicine & Life Sciences

Chemical Compounds