Preclinical correction of human Fanconi anemia complementation group A bone marrow cells using a safety-modified lentiviral vector

P. S. Becker, J. A. Taylor, G. D. Trobridge, X. Zhao, B. C. Beard, S. Chien, J. Adair, D. B. Kohn, J. E. Wagner, A. Shimamura, H. P. Kiem

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