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Pegvaliase for the treatment of phenylketonuria: Results of a long-term phase 3 clinical trial program (PRISM)
PRISM investigators
Molecular & Medical Genetics
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peer-review
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Dive into the research topics of 'Pegvaliase for the treatment of phenylketonuria: Results of a long-term phase 3 clinical trial program (PRISM)'. Together they form a unique fingerprint.
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Medicine & Life Sciences
pegvaliase
Phenylketonurias
Phase III Clinical Trials
Phenylalanine
Anaphylaxis
Anabaena variabilis
Phenylalanine Ammonia-Lyase
Therapeutics
Hypersensitivity
cinnamic acid
National Institute of Allergy and Infectious Diseases (U.S.)
Injection Site Reaction
Enzyme Therapy
Medical Genetics
Safety
Food Hypersensitivity
Chemical Compounds
Phenylalanine
Blood
Allergies
cinnamic acid
Titration
Genetics
Genomics
Ammonia