First-in-human mutation-targeted siRNA phase Ib trial of an inherited skin disorder

Sancy A. Leachman, Robyn P. Hickerson, Mary E. Schwartz, Emily E. Bullough, Stephen L. Hutcherson, Kenneth M. Boucher, C. David Hansen, Mark J. Eliason, G. Susan Srivatsa, Douglas J. Kornbrust, Frances J.D. Smith, Wh Irwin McLean, Leonard M. Milstone, Roger L. Kaspar