Compounds that correct F508del-CFTR trafficking can also correct other protein trafficking diseases: an in vitro study using cell lines.

Heidi M. Sampson, Hung Lam, Pei Chun Chen, Donglei Zhang, Cristina Mottillo, Myriam Mirza, Karim Qasim, Alvin Shrier, Show Ling Shyng, John W. Hanrahan, David Y. Thomas

Research output: Contribution to journalArticlepeer-review

29 Scopus citations

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Medicine & Life Sciences