Adeno-associated viral vector-mediated gene transfer of human blood coagulation factor IX into mouse liver

Hiroyuki Nakai, Roland W. Herzog, J. Nathan Hagstrom, Johannes Walter, Szu Hao Kung, Edmund Y. Yang, Shing Jen Tai, Yuichi Iwaki, Gary J. Kurtzman, Krishna J. Fisher, Peter Colosi, Linda B. Couto, Katherine A. High