Network
Richard S. Finkel
- Children's Hospital of Philadelphia
- University of Pennsylvania
- Nemours
- University of Central Florida
- Florida College
- Nemours Children's Clinic
- Division of Neurology
- Department of Neurology
- Nemours Children's Hospital
- Division of Neurology
- Division of Pediatric Neurology
- St. Jude Children Research Hospital
- The Children's Hospital of Philadelphia
External person
Krista Vandenborne
- University of Florida
- Department of Physical Therapy
- Departments of Physical Therapy
- Department of Physical Therapy
External person
Gihan I. Tennekoon
- University of Pennsylvania
- Oregon Health and Science University
- The Children's Hospital of Philadelphia
External person
Glenn A. Walter
- University of Florida
- Departments of Physiology and Functional Genomics
- Department of Physiology and Functional Genomics
External person
Rebecca J. Willcocks
- University of Florida
- Department of Physical Therapy
- Departments of Physical Therapy
- Department of Physical Therapy
External person
Claudia R. Senesac
- University of Florida
- Departments of Physical Therapy
- Department of Physical Therapy
- Department of Physical Therapy
- Department of Statistics
- University of Florida
External person
Sean C. Forbes
- University of Florida
- Departments of Physical Therapy
- Department of Physical Therapy
- Department of Physical Therapy
External person
Donovan J. Lott
- University of Florida
- Departments of Physical Therapy
- Department of Physical Therapy
- Department of Physical Therapy
- Rady Children's Hospital
External person
William T. Triplett
- University of Florida
- Departments of Physical Therapy
- Department of Physiology and Functional Genomics
- Departments of Physiology and Functional Genomics
- Department of Physical Therapy
- Department of Physical Therapy
External person
H. L. Sweeney
- University of Texas Southwestern Medical Center
- University of Pennsylvania
- University of Florida
- Department of Physiology
- Department of Pharmacology and Therapeutics
External person
Michael J. Daniels
- University of Florida
- University of Texas at Austin
- Departments of Integrative Biology and Statistics and Data Sciences
- Department of Statistics
- Section of Integrative Biology
- University of Florida
External person
Barry Russman
- Oregon Health and Science University
- Shriners Hospital for Children-Portland
- Shriners Hospitals for Children
- Portland Shriner's Hospital
- Shriners Hospital for Children
- Oregon Health and Science University
- Department of Surgery
- Department of Pediatric Neurology
- Molecular and Medical Genetics, Pediatrics and Neurology
- Department of Neurology
- Pediatric Neurology
- Division of Neurology
- Shriner's Hospital
- Child Development/Rehab. Center
- Shriners Hospital
- Children's Hospital New Orleans
External person
Ann T. Harrington
- University of Pennsylvania
- Department of Physical Therapy
- University of Florida
- Arcadia University
- The Children's Hospital of Philadelphia
External person
Dah Jyuu Wang
- University of Pennsylvania
- Department of Radiology
- University of Florida
- Department of Radiology
- The Children's Hospital of Philadelphia
External person
Craig M. McDonald
- University of California Office of the President
- University of California at Davis
- Department of Physical Medicine and Rehabilitation
- University of California
- Department of Physical Medicine and Rehabilitation
External person
Barry J. Byrne
- University of Florida
- Department of Pediatrics and Molecular Genetics and Microbiology
- Department of Pediatrics
- Dept. of Molec. Genet./Microbiology
- Department of Pediatrics
- Powell Gene Therapy Center
- Department of Molecular Genetics and Microbiology
External person
Julie Parsons
- University of Colorado Denver
- University of Colorado Anschutz Medical Campus
External person
Alison M. Barnard
- University of Florida
- Department of Physical Therapy
- Departments of Physiology and Functional Genomics
External person
S. T. Iannaccone
- Baylor College of Medicine
- University of Cincinnati School of Medicine
- University of Cincinnati
- University of Texas Southwestern Medical Center
- Institute for Molecular Genetics
- Department of Neurology
External person
Basil T. Darras
- Harvard University
- Department of Neurology
- Departments of Neurology
- Department of Neurology
- Boston Children's Hospital
External person
Anne M. Connolly
- St. Louis Children's Hosp., W.
- Washington University St. Louis
- St. Louis Children’s Hospital
- Department of Neurology
- Department of Neurology
- Department of Neurology
- Department of Pediatrics
- Division of Pediatric and Developmental Neurology
External person
Nancy Kuntz
- Children's Memorial Hospital
- Ann and Robert H. Lurie Children's Hospital of Chicago
- Department of Pediatrics
External person
M. Ryan
- Royal Children's Hospital
- Murdoch Children's Research Institute
- University of Melbourne
External person
Janbernd Kirschner
- University of Freiburg
- Department of Neuropediatrics and Muscle Disorders
- Freiberg University of Mining and Technology
External person
Francesco Muntoni
- University College London
- UCL Institute of Child Health and Great Ormond Street Hospital for Children NHS Foundation Trust
External person
Már Tulinius
- University of Gothenburg
- Department of Pediatrics
- Sahlgrenska University Hospital
External person
Eugenio Mercuri
- Catholic University of the Sacred Heart
- Department of Pediatric Neurology
External person
Claudia A. Chiriboga
- Columbia University
- Departments of Neurology
- Department of Neurology
- Cornell University
External person
Anna Mayhew
External person
Chris Coffey
- University of Iowa
- Department of Biostatistics
- Data Coordinating Center
- Banner Health
- University of Pennsylvania
External person
Ai Sakonju
- University of Utah
- SUNY Upstate Medical University
- Departments of Neurology and Pediatrics
- Department of Neurology
- Department of Pediatrics
External person
Steve Kolb
- Ohio State University
- Department of Neurology
- Department of Biological Chemistry and Pharmacology
- Department of Neurology
External person
H. Arora
- University of Florida
- Department of Physical Therapy
- Department of Physical Therapy
- Departments of Physical Therapy
External person
Enrico Bertini
- Bambino Gesus Children's Hospital
- IRCCS Ospedale pediatrico Bambino Gesù - Roma
- Unit of Molecular Medicine
- Oregon Health and Science University
- Department of Molecular and Medical Genetics
External person
Kevin M. Flanigan
- Department of Pediatrics, Ohio State University
- Ohio State University
- Nationwide Children’s Hospital
- Center for Gene Therapy
External person
Kristin Krosschell
- Northwestern University
- Departments of Physical Therapy
- Department of Physical Therapy and Human Movement Sciences
External person
Susan D. Apkon
- University of Washington
- University of Colorado Anschutz Medical Campus
- Seattle Children's Hospital
External person
Kathryn J. Swoboda
- University of Utah
- Harvard University
- Departments of Neurology and Pediatrics
- Department of Neurology
- Department of Neurology
- Department of Pediatrics
- Department of Neurology
- Department of Pediatrics
- Ann Romney Center for Neurologic Disease
- Massachusetts General Hospital
- Massachusetts General Hospital Cancer Center
- Boston Children's Hospital
External person
J. Dastgir
- Goryeb Children's Hospital
- National Institutes of Health
- Columbia University
- Goryeb Children's Hospital
External person
Katherine D. Mathews
- University of Iowa
- University of Iowa Hospital/Clinics
- University of Iowa
- Department of Pediatrics
- Departments of Pediatrics
- Division of Neurology
- Department of Pediatrics
External person
J. Brandsema
- University of Florida
- University of Pennsylvania
- The Children's Hospital of Philadelphia
External person
Thomas Voit
- Duke University Medical Center
- Duke University
- University College London
- Department of Pediatrics
- Department of Pediatrics
- National Institute for Health and Care Research
External person
Michelle McGovern
- Harvard Partners
- Harvard University
- Department of Neurology
- Clinical Coordinating Center
- Department of Neurology
- Ann Romney Center for Neurologic Disease
- Massachusetts General Hospital
External person
Richard Barohn
- University of Kansas
- Department of Neurology
- Department of Neurology
- Medical Center
- University of Texas Southwestern Medical Center
- Department of Neurology
- Medical Center
- University of Kansas
- University of Kansas
- University of Kansas Hospital & Medical Center
- Children's Mercy Hospitals and Clinics
External person
Ishu Arpan
- University of Florida
- Oregon Health and Science University
- Department of Neurology
- Departments of Physical Therapy
- Department of Neurology
- Advanced Imaging Research Center
External person
Jon Yankey
- University of Iowa
- University of Rochester
- Department of Biostatistics
- Data Coordinating Center
- Clinical Trials Coordination Center
- Cleveland Clinic Foundation
External person
Sandra P. Reyna
- University of Utah
- Harvard University
- Biogen IDEC
- Departments of Neurology and Pediatrics
- Department of Neurology
- Department of Neurology
- Department of Pediatrics
- Ann Romney Center for Neurologic Disease
- Massachusetts General Hospital
External person
W. David Arnold
- Ohio State University
- Department of Neurology
- Department of Physical Medicine and Rehabilitation
- Department of Neurology and Physical Medicine and Rehabilitation
- Department of Neurology
External person
D. C. Files
- Johns Hopkins University
- Division of Pulmonary and Critical Care
- McKusick-Nathans Institute of Genetic Medicine
- Wake Forest University
- IVY Network
External person
Kristi J. Jones
- University of Sydney
- Department of Clinical Genetics
- The Children's Hospital at Westmead
External person
Harvey Singer
- University of Rochester Medical Ctr.
- Johns Hopkins University
- Johns Hopkins University School of Medicine
- University of Rochester
- Pediatric Neurology
- Department of Neurology
- Department of Neurology
- Department of Neurology
- Department of Neurology
External person
E. Andres-Mateos
- Johns Hopkins University
- McKusick-Nathans Institute of Genetic Medicine
- McKusick-Nathans Institute of Genetic Medicine
External person
Timothy Lotze
- Baylor College of Medicine
- Texas Children's Cancer Center
- Department of Neurology
- Texas Children's Hospital Houston
External person
T. T. Duong
- Stanford University
- Children's National Medical Center
- Cincinnati Children's Hospital Medical Center
External person
J. L. Simmers
- Johns Hopkins University
- McKusick-Nathans Institute of Genetic Medicine
- McKusick-Nathans Institute of Genetic Medicine
External person
Tom Prior
- Ohio State University
- Laboratory Quality Assurance Committee
- American College of Medical Genetics
- Ohio State Wexner Medical Center
- Department of Molecular Pathology
- Department of Pathology
- Division of Human Cancer Genetics
- Molecular Subcommittee
- ACMG Laboratory Quality Assurance Committee
- ACMG Laboratory Quality Assurance Molecular Subcommittee
- Department of Pathology
- American College of Medical Genetics
External person
M. K. James
External person
Isabelle Desguerre
- Hôpital Necker Enfants Malades
- Hopital Necker-Enfants Malades
- Université Paris 5
- Department of Pediatric Neurology
- Department of Pediatric Neurology
- Université Paris Cité
External person
Brenda L. Wong
- University of Massachusetts Medical School
- Cincinnati Children's Hospital Medical Center
External person
Samantha R. Renusch
- Ohio State University
- Department of Biological Chemistry and Pharmacology
External person
Arthur H.M. Burghes
- Ohio State University
- Department of Biological Chemistry and Pharmacology
External person
Seward B. Rutkove
- Harvard University
- Department of Neurology
- Department of Neurology
- Beth Israel Deaconess Medical Center
External person
R. D. Cohn
- Johns Hopkins University
- Department of Neurology
- McKusick-Nathans Institute of Genetic Medicine
- Department of Pediatrics
- Department of Pediatrics
- McKusick-Nathans Institute of Genetic Medicine
- Department of Neurology
- University of Toronto
External person
Linda Lowes
External person
Merit E. Cudkowicz
- Department of Neurology
- Harvard University
- Massachusetts General Hospital
External person
Lindsay N. Alfano
External person
A. Soleimani
- Johns Hopkins University
- McKusick-Nathans Institute of Genetic Medicine
- McKusick-Nathans Institute of Genetic Medicine
External person
Melissa D. Svoboda
- Oregon Health and Science University
- University of Texas at Austin
- University of Texas System
External person
Elena S. Mazzone
External person
Brenda L. Wong
- Cincinnati Children's Hospital Medical Center
- Cincinnati Children's Hospital and Medical Center
- Departments of Neurology and Pediatrics
- Division of Pediatric Neurology
- University of Massachusetts Medical School
External person
R. Marx
- Johns Hopkins University
- McKusick-Nathans Institute of Genetic Medicine
- McKusick-Nathans Institute of Genetic Medicine
External person
Jacinda B. Sampson
- University of Utah
- Department of Neurology
- National Institutes of Health, Bethesda
- National Institutes of Health
- Stanford University
External person
K. J. Rose
- The Children's Hospital at Westmead
- University of Pennsylvania
- The Children's Hospital of Philadelphia
External person
Vicki L. Mcgovern
- Ohio State University
- Department of Biological Chemistry and Pharmacology
External person
L. Nelson
- National Institutes of Health
- Cincinnati Children's Hospital Medical Center
- University of Texas Southwestern Medical Center
External person
N. Rausch
External person
Marcus Krüger
- University of Freiburg
- Cologne Excellence Cluster on Cellular Stress Responses in Aging-Associated Diseases (CECAD)
External person
J. Cappell
External person
K. M. Carroll
External person
M. Souris
External person
F. Trucco
External person
Leslie A. Leinwand
- University of Colorado Boulder
- Department of Molecular
- University of Colorado Anschutz Medical Campus
External person
L. Weimer
External person
W. C. Virginia
- St George's University Hospitals NHS Foundation Trust
- Queen Mary's Hospital
External person
P. Ghosh
External person
Loren D.M. Pena
- University of Cincinnati
- National Institutes of Health
- Cincinnati Children's Hospital Medical Center
- Duke University
- University of Pittsburgh
External person
C. Manzitti
External person
Y. H. Ju
External person
B. Taicher
External person
H. Jo
External person
S. Stein
External person
J. Lee
External person
Alan Pestronk
- Washington University St. Louis
- Washington Univ. Med. Ctr., 660 S.
- Department of Neurology
- Department of Neurology
- Department of Neurology
External person
P. T. Golumbek
External person
A. Farrow-Gillespie
External person
N. Miller
External person
H. Verhelst
External person
A. Herbert
External person
M. del Pilar Tirado Requero
External person
A. Pechmann
External person
N. Y. Ki
External person
S. A. Choi
External person
J. D. Endsley
External person
M. N. Chui-San
External person
Y. Tanaka
External person
S. Chan
External person
H. I. Shin
External person
N. Berthon-Jones
External person
Mark Tarnopolsky
- McMaster University
- McMaster University Medical Center
- Department of Pediatrics
- Department of Medicine
- Neuromuscular and Neurometabolism Unit
- Division of Neuromuscular and Neurometabolic Disorders
- Hamilton Health Sciences
External person
Jean Teasley
External person
J. B. Bodensteriner
External person
L. Sanabria
External person
H. Lee Sweeney
External person
S. Ito
External person
Hoda Abdel-Hamid
External person
C. S. Davis
External person
A. C. Chung
External person
PH Lister
External person
Talal Alabduljalil
- Oregon Health and Science University
- Oregon Health and Science University
- Casey Eye Institute
- Albahar Eye Center
- Ibn Sina Hospital
- Casey Eye Institute
External person
Christophe Hourdé
- Sorbonne Université
- Institut de Myologie; CNRS UMR 7215; INSERM
- Universite Pierre et Marie Curie
- CNRS Centre National de la Recherche Scientifique
External person
M. Eckenweiler
External person
M. M. Martinez Moreno
External person
K. Hirasawa
External person
F. Munell Casadesus
External person
S. Paulose
External person
J. Flickinger
External person
I. J.K. Janice
External person
C. Kelly
External person
E. De Vos voor
External person
S. Nagata
External person
J. Pisco Domingos
External person
V. G. Haliloglu
External person
T. Gidaro
External person
Robert Leshner
External person
K. Booker
External person
S. Gilabert
External person
M. Gallardo
External person
M. Shichiji
External person
S. Goldman
External person
I. Woodcock
External person
Robert D. Steiner
- Marshfield Clinic
- Oregon Health and Science University
- University of Wisconsin-Madison
- Oregon Clinic
- Oregon Health and Science University
- CDRCF
- Marshfield Clinic Research Foundation, University of Wisconsin
- Oregon Health and Sciences University
- University of Washington
- Translational Research Institute
- AB SCIEX
- CDRC-F
- Oregon Health Sciences University
- CDRC-P
- AB Sciex
- Child Development/Rehab. Center
- Chemistry and Consumables R and D
- Department of Molecular and Medical Genetics
- Department of Pediatrics
- Department of Pathology
- Department of Pediatrics
- Department of Pediatrics
- Dept. of Physiology and Pharmacology, L334
- Department of Surgery
- Department of Molecular Medical Genetics
- Department of Pediatrics
- Institute on Development and Disability
- Department of Pediatrics
- Departments of Pediatrics and Molecular and Medical Genetics
- Division of Pediatric Critical Care Medicine
- Departments of Pediatrics and Molecular and Medical Genetics
- Institute on Development and DisabilityOregon Health and Science UniversityPortland
- Institute on Development and Disability
- Department of Pédiatrie and Child Development
- Section of Clinical Nutrition
- Department of Medicine
- Division of Endocrinology
- Infectious Disease
- Department of Pediatrics
- Depts. Pediat. Molec. Med. Genet.
- Center for Human Genetics
- Child and Adolescent Psychiatrist
- Department of Pediatrics
- Department of Pediatrics
- Department of Pediatrics and Molecular and Medical Genetics
- Department of Pediatrics
- Science University
- Department of Pediatrics, Oregon Health
- Department of Molecular and Medical Genetics
- Department of Pediatrics
- School of Medicine
- The Oregon Clinic
- University of Wisconsin-Stevens Point
- Department of Medicine
- University of Wisconsin
- Department of Physiology and Pharmacology
- Dept. of Med. Genetics and Neurology
- Douglas Hospital Research Center
- Danaher Corporation
- McGill University
External person
P. Jachertz
External person
J. Kitsuwa-Lowe
External person
E. Gargaun
External person
S. I. Pascual Pascual
External person
H. C.C. Alvin
External person
T. O. Crawford
- Johns Hopkins University
- Departments of Neurology and Pediatrics
- Department of Neurology
External person
A. Constantinescu
External person
Ksenija Gorni
External person
A. Y. Manzur
- Great Ormond Street Hospital
- University College London
- Dubowitz Neuromuscular Centre for Congenital Muscular Dystrophies and Myopathies
- UCL Institute of Child Health and Great Ormond Street Hospital for Children NHS Foundation Trust
External person
F. Shu
External person
C. Milleson
External person
L. Case
External person
S. Chidambaranathan
External person
Merit Cudkowicz
- Harvard Partners
- Harvard University
- Department of Neurology
- Clinical Coordinating Center
- Department of Neurology
- Neurology Clinical Trials Unit
- Department of Neurology
- Department of Neurology
- Department of Neurology
- Ann Romney Center for Neurologic Disease
- Massachusetts General Hospital
External person
E. S. Schroers
External person
E. Serdaroglu
External person
Gareth A. Harman
- Oregon Health and Science University
- Oregon Health and Science University
- Casey Eye Institute
- Casey Eye Institute
External person
Yoram Nevo
External person
John M. Freeman
- Johns Hopkins University
- Department of Neurology
- Department of Pediatrics
External person
S. Garcia Guixot
External person
M. Civitello
External person
K. Watson
External person
G. Gili
External person
Daehak ro Jongno-gu
External person
Eric H. Kossoff
- Johns Hopkins University
- David M. Rubenstein Child Health Building
- Department of Neurology
- Department of Pediatrics
- Neurology and Pediatrics
- John M. Freeman Pediat. Epilepsy C.
- Johns Hopkins
External person
K. Engelstad
External person
Anne M. Connolly
External person
G. VanderVeen
External person
T. Kandula
External person
Y. Ito
External person
A. Koka
External person
G. D'Souza
External person
Sanjay Sisodiya
- University College London
- Epilepsy Society
- Epilepsy Society
- Department of Clinical and Experimental Epilepsy
- Chalfont Centre for Epilepsy
- Epilepsy Society
- Chalfont Centre for Epilepsy
- Chalfont Centre for Epilepsy
External person
E. Kichula
External person
Douglas M. Sproule
External person
Jacob Hen
External person
A. Bielsky
External person
V. Vishwanathan
External person
V. Chau
External person
T. Harrington
External person
J. Marra
External person
S. Richardson
External person
R. Finkel
External person
A. F. Rucian
External person
Tyesha N. Burks
- Johns Hopkins University
- McKusick-Nathans Institute of Genetic Medicine
External person
S. Wittevrongel
External person
M. de Los Angeles Tormos Munoz
External person
Louis M. Staudt
- High ThroughPut Genomics
- National Institutes of Health
- Metabolism Branch
- NCI
- Center for Cancer Research
- NIH
- Scimentis
- National Institutes of Health
- Beckman Research Institute of City of Hope
- National Institutes of Health, Bethesda
- Metabolism Branch
- Lymphoid Malignancies Branch
- Surgery Branch
- Center for Cancer Research
- Hematopathology Section
- Metabolism Branch
- Laboratory of Pathology
- DNA Repair Section
- Department of Pathology
- Center for Cancer Research
- Division of Immunology
- Division of Cancer Treatment and Diagnosis
- Center for Cancer Research
- Laboratory of Pathology
- Scimentis
- City of Hope National Med Center
- Max Planck Institute of Psychiatry
- Ludwig Maximilian University of Munich
External person
Giacomi Pietro Comi
External person
J. Kurz
External person
Kristi J. Jones
External person
Ted Abresch
External person
S. Patnaik
External person
H. Szelag
External person
M. Oskoui
External person
N. Sponemann
External person
B. Andres
External person
Alberto Dubrovsky
External person
Stephan Schmidt
- Center for Pharmacometrics and Systems Pharmacology
- University of Florida
External person
Florian Lang
- University of Tübingen
- Department of Physiology I
- Department of Physiology II
- Department of Physiology
- Institute of Physiology
External person
W. C. Liang
External person
John Dean
External person
Volker Straub
- Newcastle University
- John Walton Muscular Dystrophy Research Centre
- Newcastle upon Tyne Hospitals NHS Foundation Trust
External person
B. C. Lim
External person
A. Khandji
External person
W. Douglas Biggar
External person
M. Kasper
External person
H. Shimomura
External person
Sarada Sakamuri
External person
Jim Pollaro
- Oregon Health and Science University
- Advanced Imaging Research Center
- Department of Medicine
External person
Saptarshi Chakraborty
- University of Florida
- University of Pennsylvania
- Division of Neurology
- The Children's Hospital of Philadelphia
External person
R. Van Der Looven
External person
K. Mizuochi
External person
A. K. Kroksmark
External person
Alison Ross
External person
B. Planas Pascual
External person
J. Coates
External person
J. H. Hsu
External person
T. Carry
External person
P. Lanteri
External person
C. Stella
External person
L. W.M. Wendy
External person
R. Gee
External person
Siddharth Banka
- University of Manchester
- Imperial College London
- Manchester Academic Health Science Centre
- Manchester Centre for Genomic Medicine, Institute of Human Development
- Imperial College Healthcare NHS Trust
- St Mary's Hospital London
- Manchester University NHS Foundation Trust
External person
P. Tacchetti
External person
R. Laine
External person
D. Benjamin
External person
J. W. Day
- Baylor College of Medicine
- Department of Neurology
- Department of Neurology
- Stanford University
External person
L. Nelson
External person
M. Mayer
External person
S. Sivo
External person
T. N. Shun
External person
Jaume Columer
External person
T. Tachikawa
External person
Ying Hu
- Neuromuscular and Neurogenetic Disorders of Childhood Section
- National Institutes of Health
- University of Pennsylvania
External person
Susan T. Iannaccone
External person
Declan O'Rourke
- Children's Health Ireland at Temple Street
- Children's University Hospital, Dublin
External person
J. Rambaud
External person
Mazen Dimachkie
- University of Kansas
- Department of Neurology
- Medical Center
- University of Texas at Austin
- Department of Neurology
- Medical Center
- University of Kansas
- University of Texas Health Science Center at Houston
- University of Kansas Hospital & Medical Center
- Children's Mercy Hospitals and Clinics
External person
M. Chadehumbe
External person
A. Takeshita
External person
Lausanne Canton de Vaud
External person
S. Borell
External person
D. Vens
External person
J. Quigley
External person
V. Selby
External person
C. Bruno
External person
D. Villano
External person
L. Schottlaender
External person
A. Lim
External person
S. M. Scuplak
External person
A. Ross
External person
S. Trest
External person
Y. S. Zeng
External person
K. Sugimoto
External person
C. Zimmerman
External person
T. Lee
External person
P. C. Chou
External person
C. Palermo
External person
Tahseen Mozaffar
- University of California at Irvine
- University of California Office of the President
- Department of Neurology
External person
D. Berry
External person
Mar Tulinius
External person
Ozlem Goker-Alpan
- O and O Alpan, LLC
- LLC
- LSD Research and Treatment Unit
- Lysosomal and Rare Disorders Research and Treatment Center
External person
M. Tanyildiz
External person
R. Arakawa
External person
E. Mirek
External person
Erik Henricson
- University of California at Davis
- Department of Physical Medicine and Rehabilitation
External person
M. Popolizio
External person
H. Kim
External person
D. Ramsey
External person
M. del Mar Garcia Romero
External person
M. M. Homi
External person
K. J. Herbert
External person
K. DeCock
External person
H. Kaneko
External person
F. Dorban
External person
K. L. De Valle
External person
M. Miki
External person
Kim Coleman
External person
Jacinda Sampson
External person
A. Frank
External person
N. Parziale
External person
M. Luigetti
External person
H. Nakatsukasa
External person
Carrolee Barlow
- NIH
- National Institutes of Health
- Salk Institute for Biological Studies
- Merck
- BrainCells Inc.
- Salk Inst. for Biological Studies
- Genetic Disease Research Branch
- Parkinson's Institute
- Parkinson's Institute
External person
T. Sato
External person
Silvia Borras
External person
M. Yildirim
External person
M. Scoto
External person
Michael James Jones
- PeaceHealth Sacred Heart Medical Center at RiverBend
- Oregon Health and Science University
- PeaceHealth Sacred Heart Riverbend Hospital
- Departments of Pediatrics
External person
N. Taniguchi
External person
E. Roland
External person
F. G. Yildiz Sarikaya
External person
C. Johnson
External person
J. Janas
External person
L. Fanelli
External person
Laurence M. Epstein
- Harvard University
- Northwell Health System
- Brigham and Women’s Hospital
External person
S. Kramer
External person
Natalia Julia Palacios
External person
Eduardo Tizzano
- Department of Clinical and Molecular Genetics
- Autonomous University of Barcelona
- Vall dHebron University Hospital
External person
M. Gibbons
- University of Colorado Denver
- University of Colorado Anschutz Medical Campus
External person
M. Pedermonte
External person
K. Mayne
External person
C. S. Ng
External person
Hanna Kolski
External person
N. Darin
External person
S. Arpin
External person
P. Fuhr
External person
V. Tahon
External person
A. Ganfuss
External person
Zosia Miedzybrodzka
- University of Aberdeen
- Medical Genetics Group
- Clinical Genetics Centre
External person
N. Fukuda
External person
Y. Chiba
External person
Yosef A. Berlow
- Oregon Health and Science University
- Department of Behavioral Neuroscience
- Advanced Imaging Research Center
External person
Y. C. Wu
External person
L. D'Argenzio
External person
S. Wider
External person
Rosaline Quinlivan
- UCL Institute of Child Health and Great Ormond Street Hospital for Children NHS Foundation Trust
External person
Brigitte Chabrol
- Centre de Référence des Maladies Héréditaires du Métabolisme
- Assistance publique - Hôpitaux de Marseille
- Hôpital d'adultes de la Timone
External person
D. Stanford
External person
T. Ikai
External person
A. G. Le Moing
External person
J. O'Brien
External person
S. Y. Kim
External person
C. Skura
External person
S. DeArmey
External person
Tom G. Marr
- Hiberna Corporation
- Institute of Arctic Biology
- University of Alaska Fairbanks
External person
Dietmar Kuhl
- Free University Berlin
- Free University of Berlin
- University of Hamburg
- Department of Biology, Chemistry, and Pharmacy
- University Medical Center Hamburg-Eppendorf
External person
O. T. Yilmaz
External person
A. Zuffi
External person
Klaus Romero
- Duchenne Regulatory Science Consortium
- Critical Path Institute
- Critical Path Institute
- Critical Path Institute
External person
A. Michoulas
External person
T. Yanagishita
External person
A. Camuto
External person
A. Della Marina
External person
R. Salazar
External person
H. Koelbel
External person