Network
Oregon Health and Sciences University
Organizational unit: University
Institute on Development and Disability
Oregon Health and Sciences University
Organizational unit: Institute
University of Florida
External organization: Academic
The Children's Hospital of Philadelphia
External organization: Medical
Oregon Health and Science University
External organization: Academic
National Institute of Neurological Disorders and Stroke
External organization: Unknown
Nemours Children's Clinic
External organization: Unknown
National Institute for Arthritis and Musculoskeletal and Skin Diseases
External organization: Unknown
University of California at Los Angeles
External organization: Academic
University of California at Davis
External organization: Academic
University of Colorado Anschutz Medical Campus
External organization: Academic
University of Iowa
External organization: Academic
Boston Children's Hospital
External organization: Medical
Johns Hopkins University
External organization: Academic
University of Pennsylvania
External organization: Academic
Nationwide Children’s Hospital
External organization: Medical
University of Florida
External organization: Unknown
Florida State University
External organization: Unknown
University of Texas Southwestern Medical Center
External organization: Academic
University of Utah
External organization: Academic
National Institute of Health National Heart, Lung, and Blood Institute
External organization: Unknown
Shriners Hospitals for Children
External organization: Medical
University of Texas at Austin
External organization: Academic
French Muscular Dystrophy Association
External organization: Unknown
Vanderbilt University
External organization: Academic
Columbia University
External organization: Academic
National Institutes of Health
External organization: Government
Children's National Medical Center
External organization: Medical
Washington University St. Louis
External organization: Academic
Catholic University of the Sacred Heart
External organization: Academic
Biogen IDEC
External organization: Corporate
University College London
External organization: Academic
Catabasis Pharmaceuticals Inc.
External organization: Unknown
Sahlgrenska University Hospital
External organization: Medical
Ohio State University
External organization: Academic
University of Kansas
External organization: Academic
PTC Therapeutics
External organization: Unknown
The National Institute of Child Health and Human Development
External organization: Unknown
Children's Memorial Hospital
External organization: Medical
SUNY Upstate Medical University
External organization: Academic
Western University
External organization: Academic
Massachusetts General Hospital
External organization: Medical
Medical University of Warsaw
External organization: Academic
Royal Manchester Children's Hospital
External organization: Medical
University of Toronto
External organization: Academic
Cure SMA
External organization: Unknown
Freiberg University of Mining and Technology
External organization: Academic
St. Jude Children Research Hospital
External organization: Medical
University of Hamburg
External organization: Academic
Duke University
External organization: Academic
Rush University
External organization: Academic
Ionis Pharmaceuticals
External organization: Corporate
National Center for Research Resources
External organization: Unknown
Beth Israel Deaconess Medical Center
External organization: Medical
KU Leuven
External organization: Academic
AVI BioPharma Incorporated
External organization: Unknown
Hacettepe University
External organization: Academic
Spinal Muscular Atrophy Foundation
External organization: Unknown
University of Pittsburgh
External organization: Academic
Royal Children's Hospital
External organization: Medical
University of Barcelona
External organization: Academic
PharmOptima, LLC
External organization: Corporate
Northwestern University
External organization: Academic
Amicus Therapeutics
External organization: Unknown
Inc.
External organization: Unknown
Rehabilitation Research Career Development Program
External organization: Unknown
National Institute of General Medical Sciences
External organization: Unknown
Phoenix Neurological Associates
External organization: Unknown
University of Michigan, Ann Arbor
External organization: Academic
Baylor College of Medicine
External organization: Academic
University of Montreal
External organization: Academic
Research to Prevent Blindness
External organization: Unknown
Ann and Robert H. Lurie Children's Hospital of Chicago
External organization: Unknown
Biogen
External organization: Unknown
Stanford University
External organization: Academic
Ludwig Maximilian University of Munich
External organization: Academic
Wellstar Health Systems
External organization: Unknown
Hiberna Corporation
External organization: Unknown
Chalfont Centre for Epilepsy
External organization: Unknown
University of Freiburg
External organization: Academic
Kinsman Foundation
External organization: Unknown
University of Calgary
External organization: Academic
University of Central Florida
External organization: Academic
University of Milan
External organization: Academic
UCB
External organization: Unknown
AveXis
External organization: Unknown
National Institute for Health and Care Research
External organization: Unknown
Université Paris Cité
External organization: Academic
SMA Foundation and Working on Walking Fund
External organization: Unknown
Parkinson's Institute
External organization: Academic
Children's University Hospital, Dublin
External organization: Unknown
Department of Neurology
External organization: Unknown
PharmaGenesis London
External organization: Unknown
University of Leicester
External organization: Academic
Rehabilitation and Regenerative Medicine
External organization: Unknown
Emory University
External organization: Academic
LLC
External organization: Unknown
Guy's and St Thomas' NHS Foundation Trust
External organization: Medical
Karolinska Institutet
External organization: Academic
Korea National Institute of Health
External organization: Government
The Children's Hospital at Westmead
External organization: Medical
Parent Project Muscular Dystrophy
External organization: Unknown
Hadassah University Medical Centre
External organization: Medical
University of Greifswald
External organization: Academic
Centre hospitalier pour enfants de l'est de l'Ontario
External organization: Medical
Slaney Family Fund
External organization: Unknown
UCB Pharmaceuticals
External organization: Unknown
Duchenne Research Fund
External organization: Unknown
Texas Children's Hospital Houston
External organization: Medical
CNRS Centre National de la Recherche Scientifique
External organization: Academic
Shriners Hospital
External organization: Unknown
Cidade Universitária–Ilha do Fundão
External organization: Unknown
University of Duisburg-Essen
External organization: Academic
Great Falls Clinic
External organization: Unknown
Catabasis Pharmaceuticals
External organization: Unknown
Pediatric Neurology
External organization: Unknown
IRCCS Ospedale pediatrico Bambino Gesù - Roma
External organization: Medical
Broad Institute
External organization: Academic
Medical Research Council/Biological Sciences Research Council
External organization: Unknown
Division of Pulmonary and Critical Care
External organization: Unknown
Departments of Neurology
External organization: Unknown
Goryeb Children's Hospital
External organization: Unknown
Cymabay Therapeutics
External organization: Unknown
University of Virginia
External organization: Academic
Indiana University Bloomington
External organization: Academic
Harvard University
External organization: Academic
Cytokinetics
External organization: Unknown
Atom International Limited
External organization: Unknown
St. George's University of London
External organization: Academic
Tulane University
External organization: Academic
University of California at Irvine
External organization: Academic
King's College Hospital
External organization: Medical
University of Utah, Utah Poison Control Center
External organization: Unknown
Hospital Luis Calvo Mackenna
External organization: Unknown
Child Neurology Center of Northwest Florida
External organization: Unknown
Children’s Hospital of Philadelphia
External organization: Unknown
U.S. Food and Drug Administration
External organization: Unknown
Parent Project Muscular Dystrophy and Duchenne Muscular Dystrophy Regulatory Science Consortium
External organization: Unknown
Cincinnati Children's Hospital Medical Center
External organization: Medical
Royal Devon & Exeter NHS Foundation Trust
External organization: Medical
University of Tübingen
External organization: Academic
University of La Laguna
External organization: Academic
Motol University Hospital
External organization: Medical
Nantes University Hospital (CHU de Nantes)
External organization: Unknown
University of Lausanne
External organization: Academic
Hôpital d'adultes de la Timone
External organization: Unknown
Inc.
External organization: Unknown
Tokyo Women's Medical University
External organization: Academic
Insys Therapeutics
External organization: Unknown
Yale University
External organization: Academic
The Cooper Companies, Inc.
External organization: Corporate
Sorbonne Université
External organization: Academic
OPKO Health, Inc.
External organization: Corporate
Manchester University NHS Foundation Trust
External organization: Medical
Institute of Motion
External organization: Unknown
Critical Path Institute
External organization: Unknown
National Science Foundation Cooperative
External organization: Unknown
National Institute for Health and Care Research
External organization: Unknown
University of Wisconsin Oshkosh
External organization: Academic
SRM Valliammai Engineering College
External organization: Academic
Hope Hospital
External organization: Medical
Hamilton Health Sciences
External organization: Medical
Pontificia Universidad Católica de Chile
External organization: Academic
University of Manchester
External organization: Academic
Foundation Fighting Blindness
External organization: Unknown
Division of Genetics
External organization: Unknown
Arcadia University
External organization: Academic
Current affiliation: Genome Medical
External organization: Unknown
University Hospitals Bristol and Weston NHS Foundation Trust
External organization: Medical
Seoul National University
External organization: Academic
Yale Pediatric Genomics Discovery Program
External organization: Unknown
Newcastle University
External organization: Academic
University of Minnesota Twin Cities
External organization: Academic
University of Massachusetts Medical School
External organization: Academic
Pfizer
External organization: Corporate
Division of Endocrinology and Diabetes
External organization: Unknown
Cook Children's Medical Center
External organization: Unknown
LLC
External organization: Unknown
Universidade de São Paulo
External organization: Academic
Vall dHebron University Hospital
External organization: Unknown
Hospital Universitario La Fe
External organization: Medical
Neuromuscular Research Center
External organization: Unknown
Seattle Children's Hospital
External organization: Unknown
Inc.
External organization: Unknown
University of Cincinnati
External organization: Academic